Thalassemia & Blood Products

Gene deletions, hemoglobin variants, and transfusion science

Hemoglobin AS Disease (Sickle Cell Trait)

The AS phenotype is heterozygous for the sickle mutation. Most of the time, patients are asymptomatic.

Exception: Severe hypoxia can trigger sickling and hemolysis even in trait carriers.

Inheritance: Autosomal recessive — both alleles must be affected for homozygous disease.

Alpha Thalassemia: The Gene Picker

Alpha thalassemia is caused by GENE DELETIONS (not point mutations). Humans have 4 alpha-globin genes. Each gene = 25% of normal hemoglobin production.

Common in: Mediterranean, African, Southeast Asian populations. Inheritance: Autosomal recessive.

Interactive Gene Picker: Delete Genes and See the Result

Click on an alpha gene to delete it. Watch how hemoglobin levels and clinical status change:

GENES REMAINING:
4 / 4
STATUS:
Normal (no disease)
HEMOGLOBIN:
12-16 g/dL

Alpha Thalassemia Minor

Genes Deleted Frequency Sedentary Active Hb Level
1 gene (3 remaining) 75% Asymptomatic Asymptomatic ~12 g/dL
2 genes (2 remaining) 50% Asymptomatic Symptomatic ~7.5 g/dL
3 genes (1 remaining) 25% Symptomatic Symptomatic 4-5 g/dL

Alpha Thalassemia Major (All 4 Genes Deleted)

0 genes remaining = unable to make ANY hemoglobin. All hemoglobin types require alpha chains.

Result: hydrops fetalis — congestive heart failure in utero. 🔑 Fetus can't make functional hemoglobin, cardiac output fails, massive fluid accumulation, incompatible with life.

Hb Barts (γ4 chains): NOT allosteric, cannot release oxygen to tissues.

HbH (β4 chains): NOT allosteric, precipitates into Heinz bodies.

Baseline labs: RBC 3.5-4.5 million, Hb/Hct 15/45%

Beta Thalassemia: Compensation Strategy

Beta thalassemia involves 2 beta-globin genes (one per chromosome). When beta genes are deleted, the body compensates by making MORE HbA2 and HbF.

Problem: HbF becomes useless after 6 months of age.

Beta Thalassemia Minor (One Gene Deleted)

Hb ~7.5 g/dL

Beta Thalassemia Major (Both Genes Deleted)

Body can ONLY make HbA2 and HbF.

Blood Products: The Catalog

Click each card to flip and see the clinical use. 9 products you need to know:

Whole Blood
Click to learn
When: Acute hemorrhage or trauma only. Why rare: Can be harmful. Contains RBCs, plasma, ALL clotting factors. Better to give specific products.
Fresh Frozen Plasma (FFP)
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What: Yellow liquid, plasma with NO RBCs. Contains: ALL clotting factors. When: Any acute bleeding disorder.
Packed RBCs (PRBCs)
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What: Only RBCs, no plasma. When: Anemic patient (thalassemia, hemorrhage). Effect: 1 unit raises Hb by 1-2 grams. Delivers 3.4g iron per unit.
Platelets
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When: Bone marrow suppression. DO NOT transfuse unless pre-op or platelets <10K. Why: Immune sensitization; alloimmunization.
DDAVP (Desmopressin)
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What: Synthetic ADH. Effect: Releases Factor V, VIII, and vWF by contracting endothelium. When: Mild Hemophilia A, Von Willebrand's disease, severe enuresis.
Factor VIII Concentrate
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When: Severe Hemophilia A bleeding. How: Made in lab (recombinant or derived from plasma). Why needed: Patient cannot produce Factor VIII.
Albumin
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5% = isotonic (volume expander). 25% = hypertonic (pulls fluids back into circulation, only if deficient). IV half-life: 6 hours. Use: Shock, low albumin.
Cryoprecipitate
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Contains: Factor VIII, fibrinogen, vWF, small amounts Factor VII. When: Moderate bleeding in Hemophilia A, vWD, fibrinogen problems. Advantage: Small volume, high concentration.
Immunoglobulins
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What: Passive immunity, blocking antibodies. When: Hypo/agammaglobulinemic patients, post-exposure prophylaxis. Effect: Immediate but temporary immunity.

Transfusion Principles

Transfuse only when symptomatic. Target hemoglobin depends on context:

1 unit PRBCs raises Hb by 1-2 grams (HCT by 3-6) and delivers 3.4g iron.

If reticulocyte count is highHigh retic = bone marrow is already compensating and producing RBCs, let the bone marrow handle it — no transfusion needed.

Any foreign protein transfusion = risk of allergic reaction.

Transfusion Reactions: The Board Traps

Anaphylaxis

Cause: Selective IgA deficiency in recipient. Patient develops anti-IgA antibodies.

Management: STOP transfusion, epinephrine, use IgA-filtered blood for future transfusions.

Acute Febrile Reaction

Cause: WBC antigens in donor blood trigger fever.

Management: Supportive care, premedicate with acetaminophen for future transfusions.

ABO Incompatibility

Most common transfusion reaction. Cause: Wrong blood type given.

Management: STOP transfusion immediately, re-type and cross-match, supportive care.

TRALI (Transfusion-Related Acute Lung Injury)

Cause: Cytokine release from donor leukocytes.

Presentation: ARDS picture (bilateral infiltrates, hypoxemia within 6 hours of transfusion).

Management: Steroids, mechanical ventilation if needed.

TACO (Transfusion-Associated Circulatory Overload)

Cause: Transfusing too fast into elderly or renal failure patients.

Management: Vigorous diuresis.

Iron Overload & Hemochromatosis

From Transfusions to Iron Poisoning

Multiple transfusions → iron overload. Why? RBCs contain heme iron, body has no excretion mechanism.

Hemosiderosis: Bone marrow overwhelmed by iron deposits.

Hemochromatosis: Iron spills into OTHER organs. 🔑 "Bronze" organs — skin gets bronze pigmentation, liver gets cirrhosis, pancreas gets diabetes, heart gets restrictive cardiomyopathy, joints get arthritis.

Organ Involvement (The "Bronze Triad")

Organ Manifestation Clinical Pearl
Skin Bronze pigmentation Early sign
Liver Bronze cirrhosis Fibrosis → cancer
Pancreas Bronze diabetes Insulin resistance
Heart Restrictive cardiomyopathy Can be fatal
Joints Arthritis (MCP 2-3) Painful

Treatment

Chelating agents: Deferoxamine, penicillamine, EDTA-BAL

Primary Hemochromatosis

Autosomal recessive. Cause: Too much iron absorption from duodenum. Associated with HLA A3 on chromosome 6.

Secondary Hemochromatosis

Cause: Too many transfusions (like in thalassemia major).

Most common cause of death in first 10 years: Infections (iron supports bacterial growth)

Most common cause of death after 10 years: CHF (iron cardiomyopathy)

Diagnostic Clue

Stain for iron usingPrussian blue binds ferric iron (Fe³⁺), turning it blue under microscopy PRUSSIAN BLUE.

Transfusion-Related Infections

Blood transfusions expose recipient to: HIV, Hep B/C/D, EBV, CMV, hemorrhagic viruses, bacteria, malaria, babesiosis, syphilis.

Test Your Knowledge

8 questions chosen randomly from a larger pool. Get them right and you'll see confetti.

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